优质数据如何重塑罕见病经济价值:迈向数万亿美元新机遇.pptx

优质数据如何重塑罕见病经济价值:迈向数万亿美元新机遇.pptx

MakingRareDiseasesCount:HowBetterDataCanUnlockaMultitrillion-DollarOpportunity

WHITEPAPER

FEBRUARY2026

Incollaborationwith

Alexion,AstraZenecaRareDiseaseDeloitte

Images:GettyImages

Contents

Foreword

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