浙江大学《遗传学》课件-chapter11 Treatment of Genetic Disease..pptVIP

What factors have kept GRx from becoming an effective treatment for genetic disease? Short-lived nature of gene therapy Immune response Problems with viral vectors Multigene disorders. Long Way to Go… … Colour blindness corrected by gene therapy Nature, Vol. 461, No. 7261, September 16, 2009 The monkeys were trained to touch a screen when they saw coloured patches - the standard Cambridge Colour Test All male squirrel monkeys (Saimiri sciureus), which naturally see the world in just two tones Dalton, a squirrel monkey treated with gene therapy, enjoys his new colour sense .Neitz L