crispr cas9基因外科手术阻止失明.pdfVIP

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DownloadedfromonFebruary17,2017-PublishedbyColdSpringHarborLaboratoryPress

Research

GenomesurgeryusingCas9ribonucleoproteinsfor

thetreatmentofage-relatedmaculardegeneration

KyoungmiKim,1,6SungWookPark,2,3,6JinHyoungKim,3SeungHwanLee,1

DaesikKim,1,4TaeyoungKoo,1Kwang-eunKim,1,4JeongHunKim,2,3,5

andJin-SooKim1,4

1CenterforGenomeEngineering,InstituteforBasicScience,Seoul08826,RepublicofKorea;2DepartmentofBiomedicalSciences,

SeoulNationalUniversityCollegeofMedicine,Seoul03080,RepublicofKorea;3FARBL

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