夏建川生物治疗与在临床肿瘤治疗中应用-1.pptVIP

一、基因治疗 基因治疗（gene therapy）——应用分子生物学的技术向有功能缺陷的细胞补充相应功能基因，以纠正或补偿其基因缺陷，从而达到治疗的目的。 对象： 体细胞 生殖细胞 The Cause of Leukemia:Insertion of activating retrovirus vector in Pro-oncogene LOM2 Locus. （二）Strategy of Gene Therapy To transfer a repair gene into a patient, the researchers must go through several steps : They must isolate the disease-related gene; It must be packaged in a vector, usually a disabled virus that cannot reproduce and cause disease, but that can act like a delivery truck to transport the gene inside the patient’cells; Once inside the body’s cells, the new gene can begin to fu