呈现戈谢病的体征和患者协变量:戈谢早期诊断共识(GED-C)德尔菲倡议的结果.pdfVIP

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呈现戈谢病的体征和患者协变量:戈谢早期诊断共识(GED-C)德尔菲倡议的结果.pdf

Presentingsignsandpatientco-variablesinGaucherdisease:

outcomeoftheGaucherEarlierDiagnosisConsensus(GED-C)

Delphiinitiative

AtulMehta,1DavidJ.Kuter,2SamS.Salek,3NadiaBelmatoug,4BrunoBembi,5JeremyBright,6

StephanvomDahl,7FedericaDeodato,8MajaDiRocco,9OzlemGöker-Alpan,10DerralynnA.Hughes,1

ElenaA.Lukina,11MaciejMachaczka,12,13EugenMengel,14AabhaNagral,15,16KimitoshiNakamura,17

AyaNarita,18BeatrizOliveri,19GregoryPastores,20JordiPérez-López,21UmaRamaswami,1IdaV.Schwartz,22

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